gene

FDA approves first gene therapy for genetic hearing loss

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The Food and Drug Administration on Thursday approved Regeneron’s Otarmeni, the first gene therapy for genetic hearing loss. Subscribe to read this story ad-free Get unlimited access to ad-free articles and exclusive content. The drugmaker said it will offer the drug for free to U.S. patients. Otarmeni is approved to treat a very rare form … Read more

They didn’t understand why their kids kept getting sick. After a rare diagnosis, a new gene therapy offered hope.

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Ava Langenhop was always sick.  From “the time she was born,” she was “just a sick baby,” the 9-year-old’s mother, Alicia Langenhop, told CBS News. She’d catch any cough or cold. Before she was two months old, she went to the hospital twice for viral infections. Ear infections were constant. Scraped knees turned into skin … Read more